· Translarna(ataluren)冲剂口服混悬液
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· STRENSIQ(asfotase alfa)皮下注射溶液剂
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· Kanuma(sebelipase alfa)注射溶液剂
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· Kanuma(sebelipase alfa concentrate for soluti...
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· Strensiq(asfotase alfa solution injection)
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· Aldurazyme 100U/ml solution for infusion(拉罗...
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· Glybera(alipogene tiparvovec)注射溶液
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· Xuriden(uridine triacetate)尿苷三乙酸口服颗粒剂
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· STRENSIQ Subcutaneous Injection(重组融合糖蛋白...
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· Ryanodex injectable suspension(纳米丹曲林钠注...
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· CARBAGLU(carglumic acid)Tablets
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· Orphacol cap(胆酸硬胶囊 CHOLIC ACID 250毫克)
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· Cholbam(cholic acid capsules)胆酸胶囊
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· Orphacol cap(胆酸硬胶囊 50毫克 cholic acid)
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· Translarna(Ataluren granules for oral suspension)
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· REPLAGAL FOR INTRAVENOUS(阿尔法半乳糖苷酶基因...
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· Metreleptin for Injection(重组美曲普汀注射液)
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· Normosang(hemin,人血晶素注射液)
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· 依利格鲁司特硬明胶胶囊|CERDELGA(eliglustat Cap...
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· Vpriv(velaglucerase alfa for injection)
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